Property | Value |
Working Groups | AG Cyganek, AG Hasenfuß, AG Wollnik, AG Zelarayan, AG Zimmermann |
Subproject | C04, C07, D01, D02, S01 |
Open Access | Yes |
Publication Type | Journal Article |
Peer Reviewed | Yes |
PMID | 38333672 |
DOI | 10.1016/j.omtn.2024.102123 |
Publication Year | 2024 |
Title | Preclinical evaluation of CRISPR-based therapies for Noonan syndrome caused by deep-intronic LZTR1 variants |
Journal | Molecular Therapy-Nucleic Acids |
ISSN | 2162-2531 |
eISSN | 2162-2531 |
URL | http://dx.doi.org/10.1016/j.omtn.2024.102123 |
Pages | 102123 |
Issue | 1 |
Volume | 35 |
Journal Abbreviation | Mol Ther-Nucl Acids |
Authors | Knauer C, Haltern H, Schoger E, Kügler S, Roos L, Zelarayán LC, Hasenfuss G, Zimmermann W, Wollnik B, Cyganek L |
First Author | Knauer C |
Last Author | Cyganek L |
Scholia | Wikidata-based representation at Scholia |
External Resources
829https://prod.mbexc.uni-goettingen.de/literature/publications/829
Published Data Registry entry (MBExC)
1/399https://mbexc.uni-goettingen.de/archive/1/399
Research Data Archive MBExC (supplemental material)
Q129438068https://www.wikidata.org/wiki/Q129438068
Wikidata ID